Full Application is only allowed following approval of your pre-application. Please refer to the RFA for instructions and requirements for this submission located on our website at: http://www.med.upenn.edu/orphandisease/rare-disease-overview.html File names: ALL files to be uploaded should start with the LAST NAME of the PI followed by the brief name of the document. Examples: SMITH CV, SMITH Cover Page, SMITH Budget Questions regarding the scientific content of projects should be sent to Ashley Winslow at awinslow@upenn.edu. Administrative queries should be sent to Samantha Charleston at scharle@upenn.edu. Thank you, James M. Wilson, M.D., Ph.D. Rose H. Weiss Professor and Director, Orphan Disease Center Professor of Medicine and Pediatrics Director, Gene Therapy Program
PDF only
PDF. If more than one biosketch is being submitted, please combine into one PDF.
PDF file only - combine budget and justification into one PDF
Combine Research Plan and Bibliography into one PDF.
Combine all Appendix materials into one PDF. Limited to 5 pages of supplemental information pertaining to proposal or preliminary data only; a maximum of 3 relevant reprints are also acceptable. Include IRB and/or IACUC approval letters if relevant.